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Rare Disease
First-in-class antibody targeting NETosis
Brain Endothelium-Targeted Therapy for Cerebral Cavernous Malformations
Innovative approach to treat ALS using a novel small molecule target
Small molecule and enzymatic approaches to revert aberrant phase transitions in neurological disorders
CurIOS: Novel mRNA Therapeutics for Virally-driven Cancers
Development of a New Class of Therapeutics to Treat Poisoning Diseases
Identification of small molecules tuning phase transitions to treat neurological disorders
Rosevix (Rosziqumab) A ROS1 Biologic for Invasive Cancers
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