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Rare Disease

Rare Disease

First-in-class antibody targeting NETosis

Brain Endothelium-Targeted Therapy for Cerebral Cavernous Malformations

Innovative approach to treat ALS using a novel small molecule target

Small molecule and enzymatic approaches to revert aberrant phase transitions in neurological disorders

CurIOS: Novel mRNA Therapeutics for Virally-driven Cancers

Development of a New Class of Therapeutics to Treat Poisoning Diseases

Identification of small molecules tuning phase transitions to treat neurological disorders

Rosevix (Rosziqumab) A ROS1 Biologic for Invasive Cancers

Neurolexa Therapeutics

Virtus Therapeutics

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