Skip to main content

Rare Disease

Rare Disease

Treating Epilepsy in an Orphan Genetically-Defined Disorder, Tuberous Scelerosis Complex (TSC)

Antibody-mediated gene editing and DNA/RNA delivery

Sulabha Biopharmaceuticals

"Precision Inhibition of Class IIA Histone Deacetylases for Pulmonary Arterial Hypertension"

Thyron Pharmaceuticals

Sulabha Biopharmaceuticals

Subscribe to Rare Disease