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Orphan

Orphan

Development of a novel, phosphospecific alpha-synuclein antibody as a therapeutic for MSA​

Novel Mechanism to Treat Neurodegenerative Diseases

Best In Class Ferroptosis Inhibitors in Friedrich's Ataxia

Identification of small molecules tuning phase transitions to treat neurological disorders

Luna Bioscience, Inc

Rosevix (Rosziqumab) A ROS1 Biologic for Invasive Cancers

Neurolexa Therapeutics

Treating Epilepsy in an Orphan Genetically-Defined Disorder, Tuberous Scelerosis Complex (TSC)

Direct intralesional mTOR inhibition for targeted treatment of sporadic and syndromic venous and lymphatic malformations

NCS1 - A New Target for Mood Disorders and Wolfram Syndrome

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